Micro-dystrophin gene therapy demonstrates long-term cardiac efficacy in a severe Duchenne muscular dystrophy model
Investigators
Arden B Piepho
Jeovanna Lowe
Laurel R Cumby
Lisa E Dorn
Dana M Lake
Neha Rastogi
Megan D Gertzen
Sarah L Sturgill
Guy L Odom
Mark T Ziolo
Federica Accornero
Jeffrey S Chamberlain
Jill A Rafael-Fortney
Filters: 2023